Sanofi SNY announced that the FDA has granted orphan drug designation to its investigational drug, riliprubart, for the ...

The Inflation Reduction Act includes an exemption for orphan drugs for a single indication, but experts say this is far from ...

The U.S. FDA has granted orphan drug designation for Eli Lilly's olomorasib for treatment of KRAS G12C-mutant non-small cell ...

Riliprubart is an immunoglobulin G4 humanized antibody that is designed to selectively inhibit activated C1s in the classical complement pathway of the innate immune system.

Enrollment in company’s first-of-its-kind placebo-controlled Phase 2 study to evaluate the efficacy of crofelemer for ...

The biopharma industry has hit a setback in its ambition to leverage President Donald Trump’s “big, beautiful bill” to amend ...

Senate Republicans released their version of the Trump administration’s “One Big Beautiful Bill Act” on Monday with a few ...

AIDS orphans and vulnerable children are without support since the U.S. cut foreign assistance. A pastor has been frantically trying to find meds for an HIV-positive orphan who can no longer get them.

In the wake of U.S. aid cuts, Pastor Billy is reminded of his twin sister's death from AIDS. He doesn't want 9-year-old Diana ...

The designation qualifies CERo and CER-1236 for certain incentives, such as FDA assistance in designing clinical trials, access to the FDA Orphan Drug Grants Program, exemption from the drug approval ...